[Routine practice data collection for exagamglogene autotemcel (sickle cell disease): Review of the study protocol (Version 1.0) and statistical analysis plan (Version 1.0) – Second addendum to Project A23-49]
Institut für Qualität und Wirtschaftlichkeit im Gesundheitswesen
Record ID 32018014614
German
Original Title:
Exagamglogen Autotemcel (Sichelzellkrankheit): Prüfung des Studienprotokolls (Version 1.0) und des statistischen Analyseplans (Version 1.0) 2. Addendum zum Projekt A23-49 (AbD-Konzept)
Details
Project Status:
Completed
URL for project:
https://www.iqwig.de/projekte/a25-82.html
Year Published:
2025
URL for published report:
https://www.iqwig.de/download/a25-82_exagamglogen-autotemcel_addendum-zum-projekt-a23-49_v1-0.pdf
English language abstract:
There is no English language summary available
Publication Type:
Full HTA
Country:
Germany
MeSH Terms
- Anemia, Sickle Cell
- Gene Editing
- Genetic Therapy
- Hematopoietic Stem Cell Transplantation
- CRISPR-Cas Systems
- Registries
- Adolescent
- Adult
Keywords
- Exagamglogene Autotemcel
- Anemia – Sickle Cell
- Adolescent
- Adult
- Registries
- Benefit Assessment
- Research Design
Contact
Organisation Name:
Institute for Quality and Efficiency in Health Care (IQWiG)
Contact Address:
IQWiG, Siegburger Str. 237, 50679 Cologne, GERMANY, Tel: +49(0)221-35685, Fax: +49(0)221-356851
Contact Email:
berichte@iqwig.de
Copyright:
Institut für Qualität und Wirtschaftlichkeit im Gesundheitswesen (IQWiG)
This is a bibliographic record of a published health technology assessment from a member of INAHTA or other HTA producer. No evaluation of the quality of this assessment has been made for the HTA database.