[Enzyme replacement therapy in lysosomal storage diseases: systematic review and budgetary impact. Update]

Paladio N, Expósito JÁ
Record ID 32018005531
Original Title: Tratamiento de sustitución enzimática en enfermedades por depósito lisosomal: revisión sistemática e impacto presupuestario. Actualización
Project Status: Completed
Year Published: 2018
English language abstract: There is no English language summary available
Publication Type: Full HTA
Country: Spain
MeSH Terms
  • Enzyme Replacement Therapy
  • Lysosomal Storage Diseases
  • Biological Therapy
  • Recombinant Proteins
  • Costs and Cost Analysis
  • Mucopolysaccharidosis I
  • Mucopolysaccharidosis II
  • Mucopolysaccharidosis VI
  • Gaucher Disease
  • Fabry Disease
Organisation Name: Agència de Qualitat i Avaluació Sanitàries de Catalunya (AQuAS)
Contact Address: Carrer de Roc Boronat, 81-95 (2a planta) ES-08005 Barcelona Spain
Contact Name: Roland Pastells Peiró
Contact Email: roland.pastells@gencat.cat
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