Advice on a potential candidate for conditional inclusion of ataluren (Translarna®) for Duchenne's muscular dystrophy

Wijma S, de Vries M
Record ID 32018001611
Dutch
Original Title: Advice on a potential candidate for conditional inclusion of ataluren (Translarna®) for Duchenne's muscular dystrophy (procedure: orphan drugs, conditionals and exceptionals)
Details
Project Status: Completed
Year Published: 2020
English language abstract: An English language summary is available
Publication Type: Other
Country: The Netherlands
MeSH Terms
  • Adolescent
  • Oxadiazoles
  • Muscular Dystrophy, Duchenne
  • Child
Contact
Organisation Name: The National Health Care Institute (ZIN, Zorginstituut Nederland)
Contact Address: Postbus 320, NL-1110 AH Diemen The Netherlands
Contact Name: Timon Sibma
Contact Email: TSibma@zinl.nl
This is a bibliographic record of a published health technology assessment from a member of INAHTA or other HTA producer. No evaluation of the quality of this assessment has been made for the HTA database.