Bezafibrate as treatment in males for Barth syndrome: CARDIOMAN, a double-blind, placebo-controlled crossover RCT
Pieles G, Steward C, Dabner L, Collet L, Culliford L, Sheehan K, Ellis L, Damin M, Sammut E, Duarte N, Burgess O, Wadey C, Williams C, Crosby J, Groves S, Searle A, Amulic B, Rice C, Bucciarelli-Ducci C, Ness A, Hamilton-Shield J, Rogers CA, Reeves BC
Record ID 32015000659
English
Original Title:
Treatment of Barth Syndrome by CARDIOlipin MANipulation (CARDIOMAN): a randomised placebo-controlled pilot trial conducted by the nationally commissioned Barth Syndrome Service
Details
Project Status:
Completed
URL for project:
https://www.journalslibrary.nihr.ac.uk/programmes/eme/1220556/#/
Year Published:
2024
URL for published report:
https://www.journalslibrary.nihr.ac.uk/eme/JDBC7982
Requestor:
NIHR Health Technology Assessment programme
English language abstract:
An English language summary is available
Publication Type:
Full HTA
Country:
England, United Kingdom
MeSH Terms
- Drug Therapy
- Bezafibrate
- Barth Syndrome
- Male
- Cardiomyopathies
Contact
Organisation Name:
NIHR Health Technology Assessment programme
Contact Address:
NIHR Journals Library, National Institute for Health and Care Research, Evaluation, Trials and Studies Coordinating Centre, Alpha House, University of Southampton Science Park, Southampton SO16 7NS, UK
Contact Name:
journals.library@nihr.ac.uk
Contact Email:
journals.library@nihr.ac.uk
This is a bibliographic record of a published health technology assessment from a member of INAHTA or other HTA producer. No evaluation of the quality of this assessment has been made for the HTA database.